RIZZUTI, MAFALDA
RIZZUTI, MAFALDA
Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti
Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
2020-11-01 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, D. Saccomanno, H.M. Moulton, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
2021-01-01 M. Bersani, M. Rizzuti, E. Pagliari, M. Garbellini, D. Saccomanno, H.M. Moulton, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients
2020-12-01 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, D. Saccomanno, N. Bresolin, G. Comi, S. Corti, M. Nizzardo
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients
2019-11-01 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, G. Comi, S. Corti, M. Nizzardo
Intracerebroventricular delivery in mice for motor neuron diseases
2017-01-01 M. Nizzardo, M. Rizzuti
Investigation of new morpholino oligomers to increase survival motor neuron protein levels in spinal muscular atrophy
2018-01-01 A. Ramirez, S.G. Crisafulli, M. Rizzuti, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo
MicroRNA expression analysis identifies a subset of downregulated miRNAs in ALS motor neuron progenitors
2018-12-01 M. Rizzuti, G. Filosa, V. Melzi, L. Calandriello, L. Dioni, V. Bollati, N. Bresolin, G.P. Comi, S. Barabino, M. Nizzardo, S. Corti
MicroRNA Metabolism and Dysregulation in Amyotrophic Lateral Sclerosis
2017-01-01 P. Rinchetti, M. Rizzuti, I. Faravelli, S. Corti
miR-129-5p: A key factor and therapeutic target in amyotrophic lateral sclerosis
2020-07-01 A. Loffreda, M. Nizzardo, A. Arosio, M. Ruepp, R.A. Calogero, S. Volinia, M. Galasso, C. Bendotti, C. Ferrarese, C. Lunetta, M. Rizzuti, A. Ronchi, O. Mühlemann, L. Tremolizzo, S. Corti, S.M.L. Barabino
Peptide-conjugated Morpholino Oligomers for treatment of Spinal Muscular Atrophy
2016-06-11 A. Ramirez, M. Rizzuti, F. Rizzo, P. Rinchetti, M. Bucchia, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo