BERSANI, MARGHERITA
BERSANI, MARGHERITA
Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti
CELL PENETRATING PEPTIDE-CONJUGATED MORPHOLINO: A NOVEL COMPOUND TO RESCUE SMA IN A SYMPTOMATIC PHASE
2022 M. Bersani
Molecular analysis of SMARD1 patient-derived cells demonstrates that nonsense-mediated mRNA decay is impaired
2022 M. Taiana, A. Govoni, S. Salani, N. Kleinschmidt, N. Galli, M. Saladini, S.B. Ghezzi, V. Melzi, M. Bersani, R. Del Bo, O. Muehlemann, E. Bertini, V. Sansone, E. Albamonte, S. Messina, F. Mari, E. Cesaroni, L. Porfiri, F.D. Tiziano, G.L. Vita, M. Sframeli, C. Bonanno, N. Bresolin, G. Comi, S. Corti, M. Nizzardo
Morpholino oligomers ameliorates pathological hallmarks in C9orf72 cellular lines and mice
2021 M. Bersani, D. Gagliardi, M. Taiana, F. Biella, M. Nizzardo, S. Corti
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
2021 M. Bersani, M. Rizzuti, E. Pagliari, M. Garbellini, D. Saccomanno, H.M. Moulton, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo
Evaluation of Morpholino oligomers therapeutic efficacy in C9orf72 ALS iPSC-derived lines
2020 M. Bersani, M. Taiana, F. Biella, M. Nizzardo, S. Ghezzi, N. Bresolin, G.P. Comi, S. Corti
Changes in pathological phenotype of C9orf72 ALS iPSC-derived lines after treatment with Morpholino oligomers
2020 M. Bersani, M. Taiana, F. Biella, M. Nizzardo, S. Ghezzi, S. Corti
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients
2020 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, D. Saccomanno, N. Bresolin, G. Comi, S. Corti, M. Nizzardo
Insights into disease mechanisms and potential therapeutics for C9orf72-related amyotrophic lateral sclerosis/frontotemporal dementia
2020 D. Gagliardi, G. Costamagna, M. Taiana, L. Andreoli, F. Biella, M. Bersani, N. Bresolin, G.P. Comi, S. Corti
Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
2020 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, D. Saccomanno, H.M. Moulton, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients
2019 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, G. Comi, S. Corti, M. Nizzardo
Molecular screening for Midichloria bacteria in hard and soft ticks (acari: Ixodida)
2016 A. Cafiso, V. Serra, M. Bersani, L. De Marco, M. Opara, D. Sassera, O. Plantard, C. Bazzocchi