PAGLIARI, ELISA

PAGLIARI, ELISA  

Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti  

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Titolo Data di pubblicazione Autori Tipo File Abstract
OPTIMIZATION OF AAV9 GENE THERAPY FOR SPINAL MUSCULAR ATROPHY WITH RESPIRATORY DISTRESS TYPE 1 USING IN VIVO DISEASE MODELS 2023 PAGLIARI, ELISA Doctoral Thesis -
Stathmins and Motor Neuron Diseases: Pathophysiology and Therapeutic Targets 2022 Delia GagliardiElisa PagliariMegi MeneriFederica RizzoGiacomo Pietro ComiStefania CortiMichela TaianaMonica Nizzardo + Article (author) -
Impairment of the neurotrophic signaling hub B-Raf contributes to motoneuron degeneration in spinal muscular atrophy 2021 Taiana, MichelaPagliari, ElisaCorti, Stefania + Article (author) -
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model 2021 Bersani M.Rizzuti M.Pagliari E.Bresolin N.Comi G. P.Corti S.Nizzardo M. + Article (author) -
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients 2020 E. PagliariM. BersaniM. RizzutiA. BordoniN. BresolinGP. ComiS. CortiM. Nizzardo + Conference Object -
Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model 2020 Pagliari E.Bersani M.Rizzuti M.Bordoni A.Bresolin N.Comi G. P.Corti S.Nizzardo M. + Conference Object -
Optimization of AAV9 gene therapy for Spinal Muscular Atrophy with respiratory distress Type 1 using in vivo disease models 2020 Pagliari E.Rinchetti P.Galli N.Taiana M.Comi GP.Corti S.Nizzardo M. + Conference Object -
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients 2019 Pagliari E.Bersani M.Rizzuti M.Bordoni A.Comi GP.Corti S.Nizzardo M. Conference Object -
IGHMBP2 related pathological pathways in Spinal Muscular Atrophy with Respiratory Distress type 1 (SMARD1) in vitro models 2019 Galli N.Taiana M.Pagliari E.Comi GP.Corti S.Nizzardo M. + Conference Object -