PAYVANDI, FLORA
PAYVANDI, FLORA
Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti
Gene therapy in hemophilia: the dawn of a new era
2025 R. Gualtierotti, A. Giachi, N. Bitto, V. La Mura, F. Peyvandi
Liver-related aspects of valoctocogene roxaparvovec gene therapy for hemophilia A: expert guidance for clinical practice
2024 V. La Mura, V. Cardinale, R. De Cristofaro, A. De Santis, G. Di Minno, L. Fabris, F. Marra, F. Morisco, F. Peyvandi, M. Pompili, C. Santoro, E. Zanon, G. Castaman
EAHAD haemophilia gene therapy clinical outcome database (EAHAD‐GTD)
2024 W. Miesbach, A. Boban, P. Chowdary, M. Coppens, M. Crato, V. Jimenez‐yuste, R. Klamroth, M. Makris, G. Mulders, F. Peyvandi
Emicizumab prophylaxis in infants with hemophilia A (HAVEN 7): primary analysis of a phase 3b open-label trial
2024 S.W. Pipe, P. Collins, C. Dhalluin, G. Kenet, C. Schmitt, M. Buri, V. Jiménez-Yuste, F. Peyvandi, G. Young, J. Oldenburg, M.E. Mancuso, K. Kavakli, A. Kiialainen, S. Deb, M. Niggli, T. Chang, M. Lehle, K. Fijnvandraat
Fitusiran prophylaxis in people with hemophilia A or B who switched from prior BPA/CFC prophylaxis: the ATLAS-PPX trial
2024 G. Kenet, B. Nolan, B. Zulfikar, B. Antmen, P. Kampmann, T. Matsushita, C. You, K. Vilchevska, C.N. Bagot, A. Sharif, F. Peyvandi, G. Young, C. Negrier, J. Chi, B. Kittner, C. Sussebach, F. Shammas, B. Mei, S. Andersson, K. Kavakli
Bleeding and thrombotic events and intensity of heparin therapy in the two first waves of COVID-19
2024 R. Rossio, M. Tettamanti, A.A. Galbussera, R. Gualtierotti, A. Giachi, A. Torri, N. Montano, A.L. Fracanzani, A. Bandera, A. Nobili, F. Peyvandi
Predictive parameters for spontaneous joint bleeding during emicizumab prophylaxis
2024 S. Arcudi, R. Gualtierotti, E. Scalambrino, M. Clerici, S. Hassan, V. Begnozzi, E.A. Boccalandro, C. Novembrino, C. Valsecchi, R. Palla, F. Peyvandi
Clinical characteristics and outcomes of vaccinated patients hospitalised with SARS-CoV-2 breakthrough infection: Multi-IPV, a multicentre study in Northern Italy
2024 A. Lombardi, S. Villa, M. Colaneri, G. Scaglione, F. Bai, B. Varisco, V. Bono, A. Vena, C. Dentone, C. Russo, M. Tettamanti, G. Renisi, G. Viero, C. Azzarà, M. Mantero, F. Peyvandi, M. Bassetti, G. Marchetti, A. Muscatello, A. Nobili, A. Gori, A. Bandera, S. Bosari, L. Scudeller, G. Fusetti, L. Rusconi, S. Dell’Orto, D. Prati, L. Valenti, S. Giovannelli, M. Manunta, G. Lamorte, F. Ferarri, D. Mangioni, L. Alagna, G. Bozzi, A. Lombardi., R. Ungaro, G. Ancona, M. Mussa, B.V. Mariani, M. Bolis, N. Iannotti, S. Ludovisi, A. Comelli, S. Biscarini, V. Castelli, E. Palomba, M. Fava, C.A. Peri, P. Saltini, T. Itri, V. Ferroni, V. Pastore, R. Massafra, A. Liparoti, T. Muheberimana, A. Giommi, R. Bianco, G.E. Chitani, C. Bobbio, I. De Matteis, A.B. Bonomi, R. Gualtierotti, B. Ferrari, R. Rossio, N. Boasi, E. Pagliaro, C. Massimo, M. De Caro, A. Giachi, N. Montano, B. Vigone, C. Bellocchi, A. Carandina, E. Fiorelli, V. Melli, E. Tobaldini, F. Blasi, S. Aliberti, M. Spotti, L. Terranova, S. Misuraca, A. D’Adda, S. Della Fiore, M. Di Pasquale, M. Contarini, M. Ori, L. Morlacchi, V. Rossetti, A. Gramegna, M. Pappalettera, M. Cavallini, A. Buscemi, M. Vicenzi, I. Rota, G. Costantino, M. Solbiati, L. Furlan, M. Mancarella, G. Colombo, G. Colombo, A. Fanin, M. Passarella, V. Monzani, C. Canetta, A. Rovellini, L. Barbetta, F. Billi, C. Folli, S. Accordino, D. Maira, C.M. Hu, I. Motta, N. Scaramellini, A.L. Fracanzani, R. Lombardi, A. Cespiati, M. Cesari, T. Lucchi, M. Proietti, L. Calcaterra, C. Mandelli, C. Coppola, A. Cerizza, A.M. Pesenti, G. Grasselli, A. Galazzi, I. Monti, A.A. Galbussera, E. Crisafulli, D. Girelli, A. Maroccia, D. Gabbiani, F. Busti, A. Vianello, M. Biondan, F. Sartori, P. Faverio, A. Pesci, S. Zucchetti, P. Bonfanti, M. Rossi, I. Beretta, A. Spolti, S. Harari, D. Elia, R. Cassandro, A. Caminati, F. Cipollone, M.T. Guagnano, D. D’Ardes, I. Rossi, F. Vezzani, A. Spanevello, F. Cherubino, D. Visca, M. Contoli, A. Papi, L. Morandi, N. Battistini, G.L. Moreo, P. Iannuzzi, D. Fumagalla, S. Leone
Rare inherited coagulation disorders: no longer orphan and neglected
2024 S. Mohsenian, P.M. Mannucci, M. Menegatti, F. Peyvandi
Risk of harm to people with haemophilia from the 2023 WHO Essential Medicines List
2024 G.F. Pierce, B. O'Mahony, R. Kaczmarek, M.W. Skinner, M. Makris, F. Peyvandi, A. Srivastava, C. Hermans, M. Crato, A. Dunn, E. Gouider, J. Mahlangu, D. Page, S.W. Pipe, M. Recht, T. Sannie, N. Schaefer, U. Schlenkrich, C. Garrido
Global Prevalence of Hereditary Thrombotic Thrombocytopenic Purpura Determined by Genetic Analysis
2024 O. Seidizadeh, A. Cairo, I. Mancini, J.N. George, F. Peyvandi
Congenital fibrinogen disorders: a retrospective clinical and genetic analysis of the Prospective Rare Bleeding Disorders Database
2024 S. Mohsenian, R. Palla, M. Menegatti, A. Cairo, A. Lecchi, A. Casini, M. Neerman-Arbez, R. Asselta, S. Scardo, S.M. Siboni, J. Blatny, O. Zapletal, J. Schved, M. Giansily-Blaizot, S. Halimeh, M.A. Daoud, H. Platokouki, H. Pergantou, R.E.G. Schutgens, M. Van Haaften-Spoor, P. Brons, B. Laros-van Gorkom, E. Van Pinxten, M. Borhany, N. Fatima, D. Mikovic, M. Saracevic, G.N. Özdemir, Y. Ay, M. Makris, C. Lockley, A. Mumford, A. Harvey, S. Austin, A. Shapiro, A. Williamson, C. Mcguinn, I. Goldberg, P. De Moerloose, F. Peyvandi
Open ADAMTS-13 conformation index predicts earlier relapse in immune-mediated thrombotic thrombocytopenic purpura
2024 L. De Waele, K. Sakai, I. Mancini, G. Sinkovits, T. Falter, T. Inoue, P. Agosti, H. Rossmann, C. Von Auer, C. Tersteeg, S.F. De Meyer, B.S. Joly, A. Veyradier, P. Coppo, R. Fijnheer, F. Peyvandi, Z. Prohászka, B. Lämmle, K. Vanhoorelbeke
Administration of gene therapy for haemophilia – The hub and spoke model and its regional differences and challenges
2024 W. Miesbach, A. Boban, P. Chowdary, M. Coppens, M. Crato, V. Jimenez‐yuste, R. Klamroth, M. Makris, G. Mulders, F. Peyvandi
Landmark endorsement of a global registry: The European Medicines Agency (EMA) Committee for Medicinal Products for Human Use (CHMP), publicly endorses World Federation of Hemophilia Gene Therapy Registry as global standard
2024 B.A. Konkle, F. Peyvandi, D. Coffin, M. Naccache, T. Youttananukorn, G.F. Pierce
Gene therapy for people with Haemophilia B: a proposed care delivery model in Italy
2024 G. Castaman, G. Di Minno, P. Simioni, A.C. Molinari, S. Siragusa, E. Baldacci, V. La Mura, A. Lupi, E.F. Grazzi, F. Peyvandi
Gender equity in hemophilia: need for healthcare, familial, and societal advocacy
2024 R. Gualtierotti, I. Garagiola, M. Mortarino, S. Spena, O. Romero-Lux, F. Peyvandi
Flow-chamber device (T-TAS) to diagnose patients suspected of platelet function defects
2024 A. Lecchi, S. La Marca, L. Padovan, M. Boscarino, F. Peyvandi, A. Tripodi
A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results
2024 C. Hermans, L.A. Valentino, C.D. Thornburg, C. Unzu, M.A. Kay, F. Peyvandi, P. Smith, W. Miesbach, W. Mckeown, G.F. Pierce, K. Khair, S.W. Pipe, K. Starcevic, M. Pillai, M. Jones, M. Chiao, I. Antonino, C. Kessler
Three-year outcomes of valoctocogene roxaparvovec gene therapy for hemophilia A
2024 B. Madan, M.C. Ozelo, P. Raheja, E. Symington, D.V. Quon, A.D. Leavitt, S.W. Pipe, G. Lowe, G. Kenet, M.T. Reding, J. Mason, M. Wang, A. von Drygalski, R. Klamroth, S. Shapiro, H. Chambost, A.L. Dunn, J. Oldenburg, S. Chou, F. Peyvandi, C.M. Millar, D. Osmond, Y. Hua, E. Dashiell-Aje, T.M. Robinson, J. Mahlangu