CASIRAGHI, VALERIA

CASIRAGHI, VALERIA  

Dipartimento di Biotecnologie Mediche e Medicina Traslazionale  

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Titolo Data di pubblicazione Autori Tipo File Abstract
U1 snRNA as a novel RNA-based therapeutic approach to modulate C9ORF72 pathology in patient-derived iPSC-motoneurons 2023 Sabrina InvernizziSerena SantangeloClaudia ColombritaValeria CasiraghiPatrizia BossolascoVincenzo SilaniAntonia Ratti + Conference Object -
Rapamycin reverts TDP-43 splicing defects and mislocalization in human in vitro models of TDP-43 proteinopathy 2023 V. CasiraghiC. ColombritaS. SantangeloS. InvernizziP. BossolascoV. SilaniA. Ratti + Conference Object -
Association of the risk factor UNC13A with survival and upper motor neuron involvement in amyotrophic lateral sclerosis 2023 Manini, AriannaCasiraghi, ValeriaBonetti, RuggeroInvernizzi, SabrinaVerde, FedericoPoletti, BarbaraSilani, VincenzoRatti, AntoniaTicozzi, Nicola + Article (author) -
Exploring epigenetic drift and rare epivariations in amyotrophic lateral sclerosis by epigenome-wide association study 2023 Peverelli, SilviaTiloca, CinziaCasiraghi, ValeriaInvernizzi, SabrinaVerde, FedericoSilani, VincenzoTicozzi, NicolaRatti, AntoniaGentilini, Davide + Article (author) -
Human in vitro models of TDP-43 proteinopathy for drug screening approaches 2022 V. CasiraghiC. ColombritaS. SantangeloS. InvernizziV. SilaniA. Ratti + Conference Object -
U1 snRNA as a novel RNA-based therapeutic approach to modulate C9ORF72 pathology in patient-derived iPSC-motoneurons 2022 S. SantangeloC. ColombritaS. InvernizziV. CasiraghiP. BossolascoV. SilaniA. Ratti + Conference Object -
Modelling ALS disease by 2D and 3D in vitro models of patient-derived iPSC 2022 P. BossolascoS. SantangeloL. LattuadaC. ColombritaV. CasiraghiS. PeverelliA. RattiV. Silani + Conference Object -
Rapamycin reverts TDP-43 splicing defects and oxidative stress-induced alterations in a human in vitro model of TDP-43 proteinopathy 2022 V. CasiraghiC. ColombritaS. SantangeloI. MiloneV. SilaniA. Ratti + Conference Object -
Rapamycin reverts TDP-43 splicing defects and mislocalization in human in vitro models of TDP-43 proteinopathy 2022 V. CasiraghiC. ColombritaS. SantangeloI. MiloneV. SilaniA. Ratti + Conference Object -
Rapamycin reverts TDP-43 splicing defects and mislocalization in human in vitro models of TDP-43 proteinopathy 2022 V. CasiraghiC. ColombritaS. SantangeloI. MiloneV. SilaniA. Ratti + Conference Object -