MEI, CECILIA
MEI, CECILIA
Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti
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Riboflavin transporter deficiency: AAV9-SLC52A2 gene therapy as a new therapeutic strategy
2025 C. Mei, V. Magliocca, X. Chen, K. Massey, A. Gonzalez-Cordero, S.J. Gray, M. Tartaglia, E.S. Bertini, S. Corti, C. Compagnucci
MODELLING RIBOFLAVIN TRANSPORTER DEFICIENCY (RTD) USING IPSC-DERIVED MODELS TO TEST GENE THERAPY EFFICACY
2025 C. Mei
| Titolo | Data di pubblicazione | Autori | Tipo | File | Abstract |
|---|---|---|---|---|---|
| Riboflavin transporter deficiency: AAV9-SLC52A2 gene therapy as a new therapeutic strategy | 2025 | Mei, CeciliaCorti, Stefania + | Article (author) | - | |
| MODELLING RIBOFLAVIN TRANSPORTER DEFICIENCY (RTD) USING IPSC-DERIVED MODELS TO TEST GENE THERAPY EFFICACY | 2025 | MEI, CECILIA | Doctoral Thesis | - |