BORRELLI, ANNA

BORRELLI, ANNA  

Dipartimento di Oncologia ed Emato-Oncologia  

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Titolo Data di pubblicazione Autori Tipo File Abstract
Italian Patients Journey for Gene Therapy in Haemophilia A 2026 Spadarella, GaiaBorrelli, AnnaMura, Vincenzo LaMancuso, Maria ElisaSantoro, CristinaSolimeno, Luigi PieroGaragiola, IsabellaPeyvandi, Flora + Article (author) -
PHARMACOLOGICAL RESCUE OF NONSENSE MUTATIONS IN CYSTIC FIBROSIS 2025 BORRELLI, ANNA Doctoral Thesis -
Awareness of individual goals, preferences, and priorities of persons with severe congenital haemophilia A for a tailored shared decision-making approach to liver-directed gene therapy. A practical guideline 2023 Peyvandi, FloraBorrelli, Anna + Article (author) -