Sfoglia per Autore
Modelling ALS disease by 3D organoids culture from human-derived iPSC
2022 N. Sorce Marta, C. Lattuada, S. Santangelo, P. Podini, S. Invernizzi, V. Casiraghi, A. Quattrini, V. Silani, A. Ratti, P. Bossolasco
Rapamycin reverts TDP-43 splicing defects and mislocalization in human in vitro models of TDP-43 proteinopathy
2022 V. Casiraghi, C. Colombrita, S. Santangelo, I. Milone, M.N. Sorce, V. Silani, A. Ratti
Rapamycin reverts TDP-43 splicing defects and mislocalization in human in vitro models of TDP-43 proteinopathy
2022 V. Casiraghi, C. Colombrita, S. Santangelo, I. Milone, M.N. Sorce, V. Silani, A. Ratti
Rapamycin reverts TDP-43 splicing defects and oxidative stress-induced alterations in a human in vitro model of TDP-43 proteinopathy
2022 V. Casiraghi, C. Colombrita, S. Santangelo, I. Milone, M.N. Sorce, V. Silani, A. Ratti
Human in vitro models of TDP-43 proteinopathy for drug screening approaches
2022 V. Casiraghi, C. Colombrita, S. Santangelo, S. Invernizzi, M.N. Sorce, V. Silani, A. Ratti
U1 snRNA as a novel RNA-based therapeutic approach to modulate C9ORF72 pathology in patient-derived iPSC-motoneurons
2022 S. Santangelo, C. Colombrita, E. Bussani, S. Invernizzi, M. Nice Sorce, V. Casiraghi, C. Lattuada, P. Bossolasco, V. Silani, F. Pagani, A. Ratti
Modelling ALS disease by 2D and 3D in vitro models of patient-derived iPSC
2022 P. Bossolasco, S. Santangelo, L. Lattuada, M.N. Sorce, C. Colombrita, V. Casiraghi, S. Peverelli, A. Ratti, V. Silani
NEK1 loss-of-function mutation impairs ciliogenesis in iPSC-motoneurons
2023 M. Nice Sorce, S. Invernizzi, C. Lattuada, S. Santangelo, V. Casiraghi, A. Brusati, A. Silva, S. Peverelli, V. Silani, P. Bossolasco, A. Ratti
Exploring epigenetic drift and rare epivariations in amyotrophic lateral sclerosis by epigenome-wide association study
2023 A. Brusati, S. Peverelli, L. Calzari, C. Tiloca, V. Casiraghi, M.N. Sorce, S. Invernizzi, E. Carbone, R. Cavagnola, F. Verde, V. Silani, N. Ticozzi, A. Ratti, D. Gentilini
Association of the risk factor UNC13A with survival and upper motor neuron involvement in amyotrophic lateral sclerosis
2023 A. Manini, V. Casiraghi, A. Brusati, A. Maranzano, F. Gentile, E. Colombo, R. Bonetti, S. Peverelli, S. Invernizzi, D. Gentilini, S. Messina, F. Verde, B. Poletti, I. Fogh, C. Morelli, V. Silani, A. Ratti, N. Ticozzi
Rapamycin reverts TDP-43 splicing defects and mislocalization in human in vitro models of TDP-43 proteinopathy
2023 V. Casiraghi, C. Colombrita, S. Santangelo, S. Invernizzi, M.N. Sorce, P. Bossolasco, V. Silani, A. Ratti
U1 snRNA as a novel RNA-based therapeutic approach to modulate C9ORF72 pathology in patient-derived iPSC-motoneurons
2023 S. Invernizzi, S. Santangelo, E. Bussani, G. Romano, C. Colombrita, V. Casiraghi, M. Nice Sorce, P. Bossolasco, V. Silani, F. Pagani, A. Ratti
Defective primary cilia in NEK1 and C9ORF72 iPSC-derived motoneurons and brain organoids
2024 S. Invernizzi, S. Santangelo, V. Casiraghi, S. Peverelli, P. Paola, Q. Angelo, V. Silani, P. Bossolasco, A. Ratti
Induced Pluripotent Stem Cell (iPSC)-derived Microglia for ALS modeling
2024 E. Pellegrini, C. Lattuada, S. Invernizzi, V. Casiraghi, S. Santangelo, V. Silani, A. Ratti, P. Bossolasco
AGGREGATION MECHANISMS OF TDP-43 PROTEIN IN RESPONSE TO STRESS IN AMYOTROPHIC LATERAL SCLEROSIS AND THERAPEUTIC APPROACHES
2024 V. Casiraghi
Modeling a novel N-terminal mutation of KIF5A gene in patient-derived iPSC-motoneurons
2024 S. Invernizzi, S. Santangelo, V. Casiraghi, P. Bossolasco, C. Fallini, S. Magri, A. Poletti, V. Silani, F. Taroni, A. Ratti
Characterization of human i3 motor neurons exposed to CSF from ALS patients stratified by C9ORF72 and UNC13A genotype
2024 V. Casiraghi, E. Pellegrini, A. Brusati, S. Peverelli, S. Invernizzi, S. Santangelo, C. Colombrita, V. Silani, A. Ratti
Characterization of human i3 motor neurons exposed to CSF from ALS patients stratified by C9ORF72 and UNC13A genotype
2024 V. Casiraghi, E. Pellegrini, A. Brusati, S. Peverelli, S. Invernizzi, S. Santangelo, C. Colombrita, V. Silani, A. Ratti
Defective primary cilia in NEK1 and C9ORF72 iPSC-derived motoneurons and brain organoids
2024 S. Invernizzi, S. Santangelo, V. Casiraghi, S. Peverelli, P. Paola, Q. Angelo, V. Silani, P. Bossolasco, A. Ratti
Induced Pluripotent Stem Cell (iPSC)-derived Microglia for ALS modeling
2024 E. Pellegrini, C. Lattuada, S. Invernizzi, V. Casiraghi, S. Santangelo, V. Silani, A. Ratti, P. Bossolasco
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