We describe 10 children with Alagille syndrome and inflammatory arthritis. In our centers, the prevalence of chronic arthritis in patients with Alagille syndrome is approximately 50 times higher compared with the general population. Arthritis was refractory to most treatment. Patients with Alagille syndrome should routinely be screened for musculoskeletal symptoms.
Alagille Syndrome and Chronic Arthritis: An International Case Series / G. Ferrara, T. Giani, S.M. Lieberman, C. Kremer, S. Hong, G. Indolfi, G. Schulert, R.Q. Cron, M.L. Mannion, S. Lapidus, W. Armbrust, E. Gonzales, E. Jacquemin, I. Kone-Paut, R. Cimaz. - In: JOURNAL OF PEDIATRICS. - ISSN 0022-3476. - 218(2020 Mar 01), pp. 228-230.
Titolo: | Alagille Syndrome and Chronic Arthritis: An International Case Series |
Autori: | CIMAZ, ROLANDO (Ultimo) |
Parole Chiave: | alagille; inflammatory arthritis; juvenile idiopathic arthritis |
Settore Scientifico Disciplinare: | Settore MED/38 - Pediatria Generale e Specialistica |
Data di pubblicazione: | 1-mar-2020 |
Rivista: | |
Tipologia: | Article (author) |
Digital Object Identifier (DOI): | http://dx.doi.org/10.1016/j.jpeds.2019.10.042 |
Appare nelle tipologie: | 01 - Articolo su periodico |
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