BUCCHIA, MONICA

BUCCHIA, MONICA  

Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti  

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Titolo Data di pubblicazione Autori Tipo File Abstract
CSF transplantation of a specific iPSC-derived neural stem cell subpopulation ameliorates the disease phenotype in a mouse model of spinal muscular atrophy with respiratory distress type 1 2019 Nizzardo, MonicaBucchia, MonicaRamirez, AgneseBresolin, NereoComi, Giacomo PietroCorti, Stefania + Article (author) -
Key role of SMN/SYNCRIP and RNA-Motif 7 in spinal muscular atrophy: RNA-Seq and motif analysis of human motor neurons 2019 Rizzo, FedericaNizzardo, MonicaVashisht, ShikhaMolteni, ErikaTaiana, MichelaSalani, SabrinaBucchia, MonicaBordoni, AndreinaFaravelli, IreneBresolin, NereoComi, Giacomo PietroCorti, Stefania + Article (author) -
TRANSPLANTATION OF A SPECIFIC NEURAL STEM CELL SUBPOPULATION AS A THERAPEUTIC APPROACH FOR AMYOTROPHIC LATERAL SCLEROSIS 2017 M. Bucchia Doctoral Thesis -
Peptide-conjugated Morpholino Oligomers for treatment of Spinal Muscular Atrophy 2016 A. RamirezM. RizzutiF. RizzoP. RinchettiM. BucchiaN. BresolinG. P. ComiS. CortiM. Nizzardo Conference Object -
Morpholino-mediated SOD1 reduction ameliorates an amyotrophic lateral sclerosis disease phenotype 2016 M. NizzardoC. SimoneF. RizzoG. UlziA. RamirezA. BordoniM. BucchiaN. BresolinG.P. ComiS. Corti + Article (author) -
Is spinal muscular atrophy a disease of the motor neurons only: pathogenesis and therapeutic implications? 2016 C. SimoneA. RamirezM. BucchiaP. RinchettiD. PapadimitriouS. Corti + Article (author) -
iPSC-derived LewisX+CXCR4+β1-integrin+ neural stem cells improve the amyotrophic lateral sclerosis phenotype by preserving motor neurons and muscle innervation in human and rodent models 2016 M. NizzardoM. BucchiaA. RamirezN. BresolinG.P. ComiS. Corti + Article (author) -
Morpholino antisense oligomer against SOD1 for amyotrophic lateral sclerosis therapy 2015 F. RizzoG. UlziA. RamirezM. BucchiaA. BordoniG. ComiS. Corti + Conference Object -
Therapeutic Development in Amyotrophic Lateral Sclerosis 2015 M. BucchiaA. RamirezC. SimoneM. NizzardoF. MagriS. DamettiS. Corti + Article (author) -
Motor neuron derivation from human embryonic and induced pluripotent stem cells: experimental approaches and clinical perspectives 2014 I. FaravelliM. BucchiaP. RinchettiM. NizzardoC. SimoneE. FrattiniS. Corti Article (author) -
Induced neural stem cells: methods of reprogramming and potential therapeutic applications 2014 G. RiboldiM. BucchiaN. BresolinG.P. ComiS. Corti + Article (author) -
IPSC-derived neural stem cells act via kinase inhibition to exert neuroprotective effects in spinal muscular atrophy with respiratory distress type 1 2014 C. SimoneM. NizzardoF. RizzoG. RiboldiS. SalaniM. BucchiaN. BresolinG.P. ComiS. Corti + Article (author) -
Clinical evaluation and cellular electrophysiology of a recessive CLCN1 patient 2013 S. LucchiariG. UlziF. MagriM. BucchiaM. ServidaG.P. Comi + Article (author) -