SIMONE, CHIARA
SIMONE, CHIARA
Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti
Differential neuronal vulnerability identifies IGF-2 as a protective factor in ALS
2016 I. Allodi, L. Comley, S. Nichterwitz, M. Nizzardo, C. Simone, J.A. Benitez, M. Cao, S. Corti, E. Hedlund
Morpholino-mediated SOD1 reduction ameliorates an amyotrophic lateral sclerosis disease phenotype
2016 M. Nizzardo, C. Simone, F. Rizzo, G. Ulzi, A. Ramirez, M. Rizzuti, A. Bordoni, M. Bucchia, S. Gatti, N. Bresolin, G.P. Comi, S. Corti
Is spinal muscular atrophy a disease of the motor neurons only: pathogenesis and therapeutic implications?
2016 C. Simone, A. Ramirez, M. Bucchia, P. Rinchetti, H. Rideout, D. Papadimitriou, D.B. Re, S. Corti
Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model
2015 M. Nizzardo, C. Simone, F. Rizzo, S. Salani, P. Rinchetti, R. Del Bo, S. Dametti, K. Foust, B. Kaspar, N. Bresolin, G. Comi, S. Corti
Motor neurons with differential vulnerability to degeneration show distinct protein signatures in health and ALS
2015 L. Comley, I. Allodi, S. Nichterwitz, M. Nizzardo, C. Simone, S. Corti, E. Hedlund
Pluripotent stem cell-based models of spinal muscular atrophy
2015 E. Frattini, M. Ruggieri, S. Salani, I. Faravelli, C. Zanetta, M. Nizzardo, C. Simone, F. Magri, S. Corti
Therapeutic Development in Amyotrophic Lateral Sclerosis
2015 M. Bucchia, A. Ramirez, V. Parente, C. Simone, M. Nizzardo, F. Magri, S. Dametti, S. Corti
MFN2-related neuropathies: clinical features, molecular pathogenesis and therapeutic perspectives
2015 G. Stuppia, F. Rizzo, G. Riboldi, R. Del Bo, M. Nizzardo, C. Simone, G.P. Comi, N. Bresolin, S. Corti
Spinal muscular atrophy phenotype is ameliorated in human motor neurons by SMN increase via different novel RNA therapeutic approaches
2015 M. Nizzardo, C. Simone, S. Dametti, S. Salani, G. Ulzi, S. Pagliarani, F. Rizzo, E. Frattini, F. Pagani, N. Bresolin, G. Comi, S. Corti
Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model
2015 M. Nizzardo, C. Simone, F. Rizzo, S. Salani, S. Dametti, P. Rinchetti, R. Del Bo, K. Foust, B.K. Kaspar, N. Bresolin, G.P. Comi, S. Corti
Stem cell transplantation for amyotrophic lateral sclerosis: therapeutic potential and perspectives on clinical translation
2014 I. Faravelli, G. Riboldi, M. Nizzardo, C. Simone, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
Cellular therapy to target neuroinflammation in amyotrophic lateral sclerosis
2014 F. Rizzo, G. Riboldi, S. Salani, M. Nizzardo, C. Simone, S. Corti, E. Hedlund
Motor neuron derivation from human embryonic and induced pluripotent stem cells: experimental approaches and clinical perspectives
2014 I. Faravelli, M. Bucchia, P. Rinchetti, M. Nizzardo, C. Simone, E. Frattini, S. Corti
Antisense Oligonucleotide Therapy for the Treatment of C9ORF72 ALS/FTD Diseases
2014 G. Riboldi, C. Zanetta, M. Ranieri, M. Nizzardo, C. Simone, F. Magri, N. Bresolin, G.P. Comi, S. Corti
Molecular, genetic and stem cell-mediated therapeutic strategies for spinal muscular atrophy (SMA)
2014 C. Zanetta, G. Riboldi, M. Nizzardo, C. Simone, I. Faravelli, N. Bresolin, G.P. Comi, S. Corti
Minimally invasive transplantation of iPSC-derived ALDHhiSSCloVLA4+ neural stem cells effectively improves the phenotype of an amyotrophic lateral sclerosis model
2014 M. Nizzardo, C. Simone, F. Rizzo, M. Ruggieri, S. Salani, G. Riboldi, I. Faravelli, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
The wide spectrum of clinical phenotypes of spinal muscular atrophy with respiratory distress type 1: a systematic review
2014 F. Porro, P. Rinchetti, F. Magri, G. Riboldi, M. Nizzardo, C. Simone, C. Zanetta, I. Faravelli, S. Corti
Molecular therapeutic strategies for spinal muscular atrophies : Current and future clinical trials
2014 C. Zanetta, M. Nizzardo, C. Simone, E. Monguzzi, N. Bresolin, G.P. Comi, S. Corti
IPSC-derived neural stem cells act via kinase inhibition to exert neuroprotective effects in spinal muscular atrophy with respiratory distress type 1
2014 C. Simone, M. Nizzardo, F. Rizzo, M. Ruggieri, G. Riboldi, S. Salani, M. Bucchia, N. Bresolin, G.P. Comi, S. Corti
Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy δ7 mouse model phenotype
2014 M. Nizzardo, C. Simone, S. Salani, M. Ruepp, F. Rizzo, M. Ruggieri, C. Zanetta, S. Brajkovic, H.M. Moulton, O. Müehlemann, N. Bresolin, G.P. Comi, S. Corti