NIZZARDO, MONICA

NIZZARDO, MONICA  

Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti  

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Risultati 1 - 20 di 116 (tempo di esecuzione: 0.004 secondi).
Titolo Data di pubblicazione Autori Tipo File Abstract
Targeting PTB for Glia‐to‐Neuron Reprogramming In Vitro and In Vivo for Therapeutic Development in Neurological Diseases 2022 Gagliardi D.Comi G. P.Ottoboni L.Nizzardo M.Corti S. + Article (author) -
Generation of two hiPSC lines (UMILi027-A and UMILi028-A) from early and late-onset Congenital Central hypoventilation Syndrome (CCHS) patients carrying a polyalanine expansion mutation in the PHOX2B gene 2022 Cuadros Gamboa A. L.Benfante R.Nizzardo M.Pelucchi P.Cardani S.Zucchi I.Corti S.Di Lascio S.Fornasari D. + Article (author) -
Stathmins and Motor Neuron Diseases: Pathophysiology and Therapeutic Targets 2022 Delia GagliardiElisa PagliariMegi MeneriFederica RizzoGiacomo Pietro ComiStefania CortiMichela TaianaMonica Nizzardo + Article (author) -
Molecular analysis of SMARD1 patient-derived cells demonstrates that nonsense-mediated mRNA decay is impaired 2022 Taiana, MichelaGovoni, AlessandraSalani, SabrinaGalli, NoemiSaladini, MatteoBersani, MargheritaDel Bo, RobertoSansone, ValeriaBresolin, NereoComi, GiacomoCorti, StefaniaNizzardo, Monica + Article (author) -
Morpholino oligomers ameliorates pathological hallmarks in C9orf72 cellular lines and mice 2021 M. BersaniD. GagliardiM. TaianaF. BiellaM. NizzardoS. Corti Conference Object -
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model 2021 Bersani M.Rizzuti M.Pagliari E.Bresolin N.Comi G. P.Corti S.Nizzardo M. + Article (author) -
Dysregulation of Muscle-Specific MicroRNAs as Common Pathogenic Feature Associated with Muscle Atrophy in ALS, SMA and SBMA: Evidence from Animal Models and Human Patients 2021 Galbiati, MariaritaTaiana, MichelaNizzardo, MonicaCorti, StefaniaPensato, VivianaMaggi, LorenzoLauria, GiuseppeBernasconi, PiaPoletti, Angelo + Article (author) -
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients 2020 E. PagliariM. BersaniM. RizzutiA. BordoniN. BresolinGP. ComiS. CortiM. Nizzardo + Conference Object -
Optimization of AAV9 gene therapy for Spinal Muscular Atrophy with respiratory distress Type 1 using in vivo disease models 2020 Pagliari E.Rinchetti P.Galli N.Taiana M.Comi GP.Corti S.Nizzardo M. + Conference Object -
Evaluation of Morpholino oligomers therapeutic efficacy in C9orf72 ALS iPSC-derived lines 2020 M. BersaniM. TaianaF. BiellaM. NizzardoN. BresolinG. P. ComiS. Corti + Conference Object -
Changes in pathological phenotype of C9orf72 ALS iPSC-derived lines after treatment with Morpholino oligomers 2020 Bersani M.Taiana M.F. BiellaM. NizzardoS. Corti + Conference Object -
Neural stem cell transplantation for neurodegenerative diseases 2020 Biella F.Rizzo F.Abati E.Nizzardo M.Bresolin N.Comi G. P.Corti S. + Article (author) -
Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model 2020 Pagliari E.Bersani M.Rizzuti M.Bordoni A.Bresolin N.Comi G. P.Corti S.Nizzardo M. + Conference Object -
Current understanding of and emerging treatment options for spinal muscular atrophy with respiratory distress type 1 (SMARD1) 2020 N. GalliM. NizzardoA. GovoniM. TaianaN. BresolinG. P. ComiS. Corti + Article (author) -
Systematic elucidation of neuron-astrocyte interaction in models of amyotrophic lateral sclerosis using multi-modal integrated bioinformatics workflow 2020 Nizzardo, MonicaPapadimitriou, DimitraRinchetti, PaolaCorti, Stefania + Article (author) -
Synaptotagmin 13 is neuroprotective across motor neuron diseases 2020 Nizzardo M.Taiana M.Rizzo F.Melzi V.Bresolin N.Comi G. P.Corti S. + Article (author) -
miR-129-5p: A key factor and therapeutic target in amyotrophic lateral sclerosis 2020 Nizzardo, MonicaRizzuti, MafaldaCorti, Stefania + Article (author) -
Animal Models of CMT2A: State-of-art and Therapeutic Implications 2020 Abati, ElenaNizzardo, MonicaBresolin, NereoComi, Giacomo PietroCorti, StefaniaRizzo, Federica + Article (author) -
Spinal muscular atrophy with respiratory distress type 1: Clinical phenotypes, molecular pathogenesis and therapeutic insights 2020 Saladini, MatteoNizzardo, MonicaGovoni, AlessandraTaiana, MichelaBresolin, NereoComi, Giacomo PCorti, Stefania Article (author) -
IGHMBP2 related pathological pathways in Spinal Muscular Atrophy with Respiratory Distress type 1 (SMARD1) in vitro models 2019 Galli N.Taiana M.Pagliari E.Comi GP.Corti S.Nizzardo M. + Conference Object -