Sfoglia per Autore
In vitro and in vivo analysis of motoneurons obtained from human-spinal muscular atrophy-induced pluripotent stem cells free of vector and transgenic sequences
2011 G. Riboldi, M. Nizzardo, M. Nardini, C. Simone, M. Falcone, D. Ronchi, C. Donadoni, S. Salani, F. Magri, N. Bresolin, G.P. Comi, S. Corti
Beta-lactam antibiotic offers neuroprotection in a spinal muscular atrophy model by multiple mechanisms
2011 M. Nizzardo, M. Nardini, D. Ronchi, S. Salani, C. Donadoni, F. Fortunato, G. Colciago, M. Falcone, C. Simone, G. Riboldi, A. Govoni, N. Bresolin, G.P. Comi, S. Corti, S. Bhatia
ALS genetic modifiers that increase survival of SOD1 mice and are suitable for therapeutic development
2011 G. Riboldi, M. Nizzardo, C. Simone, M. Falcone, N. Bresolin, G. Comi, S. Corti
Targeted gene correction of spinal muscular atrophy induced pluripotent stem cells and motoneurons as cell source for therapy
2012 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Menozzi, C. Bonaglia, F. Rizzo, F. Magri, N. Bresolin, G.P. Comi
Genetic correction of spinal muscular atrophy-induced pluripotent stem cells and motoneurons as a disease model and cell source for transplantation
2012 G. Riboldi, M. Nizzardo, M. Nardini, C. Simone, M. Falcone, D. Ronchi, C. Donadoni, S. Salani, F. Magri, F. Rizzo, M. Ranieri, A. Govoni, I. Faravelli, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
GENERAZIONE E CORREZIONE DI CELLULE STAMINALIPLURIPOTENTI INDOTTE NON VIRALI DA PAZIENTE SMA COMEMODELLO DI MALATTIA E SORGENTE PER LA TERAPIA CELLULARE
2012 C. Simone
Gene Corrected Spinal Muscular Atrophy-Induced Pluripotent Stem Cells and Motoneuron as a Model and Cell Source for Transplantation (IN8-2.002)
2012 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Riboldi, G. Menozzi, C. Bonaglia, F. Magri, N. Bresolin, G. Comi
Research advances in gene therapy approaches for the treatment of amyotrophic lateral sclerosis
2012 M. Nizzardo, C. Simone, M. Falcone, G. Riboldi, F. Rizzo, F. Magri, N. Bresolin, G. P. Comi, S. Corti
Direct reprogramming of human astrocytes into neural stem cells and neurons
2012 S. Corti, M. Nizzardo, C. Simone, M. Falcone, C. Donadoni, S. Salani, F. Rizzo, M. Nardini, G. Riboldi, F. Magri, C. Zanetta, I. Faravelli, N. Bresolin, G.P. Comi
Genetic correction of human induced pluripotent stem cells from patients with spinal muscular atrophy
2012 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Riboldi, F. Magri, G. Menozzi, C. Bonaglia, F. Rizzo, N. Bresolin, G.P. Comi
Direct reprogramming of adult somatic cells into other lineages: past evidence and future perspectives
2013 M. Nizzardo, C. Simone, M. Falcone, G. Riboldi, G.P. Comi, N. Bresolin, S.P. Corti
Molecular, genetic and stem cell-mediated therapeutic strategies for spinal muscular atrophy (SMA)
2014 C. Zanetta, G. Riboldi, M. Nizzardo, C. Simone, I. Faravelli, N. Bresolin, G.P. Comi, S. Corti
Minimally invasive transplantation of iPSC-derived ALDHhiSSCloVLA4+ neural stem cells effectively improves the phenotype of an amyotrophic lateral sclerosis model
2014 M. Nizzardo, C. Simone, F. Rizzo, M. Ruggieri, S. Salani, G. Riboldi, I. Faravelli, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
Motor neuron derivation from human embryonic and induced pluripotent stem cells: experimental approaches and clinical perspectives
2014 I. Faravelli, M. Bucchia, P. Rinchetti, M. Nizzardo, C. Simone, E. Frattini, S. Corti
IPSC-derived neural stem cells act via kinase inhibition to exert neuroprotective effects in spinal muscular atrophy with respiratory distress type 1
2014 C. Simone, M. Nizzardo, F. Rizzo, M. Ruggieri, G. Riboldi, S. Salani, M. Bucchia, N. Bresolin, G.P. Comi, S. Corti
Cellular therapy to target neuroinflammation in amyotrophic lateral sclerosis
2014 F. Rizzo, G. Riboldi, S. Salani, M. Nizzardo, C. Simone, S. Corti, E. Hedlund
Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy δ7 mouse model phenotype
2014 M. Nizzardo, C. Simone, S. Salani, M. Ruepp, F. Rizzo, M. Ruggieri, C. Zanetta, S. Brajkovic, H.M. Moulton, O. Müehlemann, N. Bresolin, G.P. Comi, S. Corti
Molecular therapeutic strategies for spinal muscular atrophies : Current and future clinical trials
2014 C. Zanetta, M. Nizzardo, C. Simone, E. Monguzzi, N. Bresolin, G.P. Comi, S. Corti
The wide spectrum of clinical phenotypes of spinal muscular atrophy with respiratory distress type 1: a systematic review
2014 F. Porro, P. Rinchetti, F. Magri, G. Riboldi, M. Nizzardo, C. Simone, C. Zanetta, I. Faravelli, S. Corti
Stem cell transplantation for amyotrophic lateral sclerosis: therapeutic potential and perspectives on clinical translation
2014 I. Faravelli, G. Riboldi, M. Nizzardo, C. Simone, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
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