Sfoglia per Autore
In vitro and in vivo analysis of motoneurons obtained from human-spinal muscular atrophy-induced pluripotent stem cells free of vector and transgenic sequences
2011-05-01 G. Riboldi, M. Nizzardo, M. Nardini, C. Simone, M. Falcone, D. Ronchi, C. Donadoni, S. Salani, F. Magri, N. Bresolin, G.P. Comi, S. Corti
Beta-lactam antibiotic offers neuroprotection in a spinal muscular atrophy model by multiple mechanisms
2011-06-01 M. Nizzardo, M. Nardini, D. Ronchi, S. Salani, C. Donadoni, F. Fortunato, G. Colciago, M. Falcone, C. Simone, G. Riboldi, A. Govoni, N. Bresolin, G.P. Comi, S. Corti, S. Bhatia
ALS genetic modifiers that increase survival of SOD1 mice and are suitable for therapeutic development
2011-10-01 G. Riboldi, M. Nizzardo, C. Simone, M. Falcone, N. Bresolin, G. Comi, S. Corti
Targeted gene correction of spinal muscular atrophy induced pluripotent stem cells and motoneurons as cell source for therapy
2012-01-01 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Menozzi, C. Bonaglia, F. Rizzo, F. Magri, N. Bresolin, G.P. Comi
Genetic correction of spinal muscular atrophy-induced pluripotent stem cells and motoneurons as a disease model and cell source for transplantation
2012-01-01 G. Riboldi, M. Nizzardo, M. Nardini, C. Simone, M. Falcone, D. Ronchi, C. Donadoni, S. Salani, F. Magri, F. Rizzo, M. Ranieri, A. Govoni, I. Faravelli, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
GENERAZIONE E CORREZIONE DI CELLULE STAMINALIPLURIPOTENTI INDOTTE NON VIRALI DA PAZIENTE SMA COMEMODELLO DI MALATTIA E SORGENTE PER LA TERAPIA CELLULARE
2012-02-08 C. Simone
Gene Corrected Spinal Muscular Atrophy-Induced Pluripotent Stem Cells and Motoneuron as a Model and Cell Source for Transplantation (IN8-2.002)
2012-04-01 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Riboldi, G. Menozzi, C. Bonaglia, F. Magri, N. Bresolin, G. Comi
Research advances in gene therapy approaches for the treatment of amyotrophic lateral sclerosis
2012-05-01 M. Nizzardo, C. Simone, M. Falcone, G. Riboldi, F. Rizzo, F. Magri, N. Bresolin, G. P. Comi, S. Corti
Direct reprogramming of human astrocytes into neural stem cells and neurons
2012-08-01 S. Corti, M. Nizzardo, C. Simone, M. Falcone, C. Donadoni, S. Salani, F. Rizzo, M. Nardini, G. Riboldi, F. Magri, C. Zanetta, I. Faravelli, N. Bresolin, G.P. Comi
Genetic correction of human induced pluripotent stem cells from patients with spinal muscular atrophy
2012-12-19 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Riboldi, F. Magri, G. Menozzi, C. Bonaglia, F. Rizzo, N. Bresolin, G.P. Comi
Direct reprogramming of adult somatic cells into other lineages: past evidence and future perspectives
2013-01-01 M. Nizzardo, C. Simone, M. Falcone, G. Riboldi, G.P. Comi, N. Bresolin, S.P. Corti
Molecular therapeutic strategies for spinal muscular atrophies : Current and future clinical trials
2014-01-01 C. Zanetta, M. Nizzardo, C. Simone, E. Monguzzi, N. Bresolin, G.P. Comi, S. Corti
The wide spectrum of clinical phenotypes of spinal muscular atrophy with respiratory distress type 1: a systematic review
2014-01-01 F. Porro, P. Rinchetti, F. Magri, G. Riboldi, M. Nizzardo, C. Simone, C. Zanetta, I. Faravelli, S. Corti
IPSC-derived neural stem cells act via kinase inhibition to exert neuroprotective effects in spinal muscular atrophy with respiratory distress type 1
2014-01-01 C. Simone, M. Nizzardo, F. Rizzo, M. Ruggieri, G. Riboldi, S. Salani, M. Bucchia, N. Bresolin, G.P. Comi, S. Corti
Minimally invasive transplantation of iPSC-derived ALDHhiSSCloVLA4+ neural stem cells effectively improves the phenotype of an amyotrophic lateral sclerosis model
2014-01-01 M. Nizzardo, C. Simone, F. Rizzo, M. Ruggieri, S. Salani, G. Riboldi, I. Faravelli, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
Motor neuron derivation from human embryonic and induced pluripotent stem cells: experimental approaches and clinical perspectives
2014-01-01 I. Faravelli, M. Bucchia, P. Rinchetti, M. Nizzardo, C. Simone, E. Frattini, S. Corti
Cellular therapy to target neuroinflammation in amyotrophic lateral sclerosis
2014-01-01 F. Rizzo, G. Riboldi, S. Salani, M. Nizzardo, C. Simone, S. Corti, E. Hedlund
Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy δ7 mouse model phenotype
2014-01-01 M. Nizzardo, C. Simone, S. Salani, M. Ruepp, F. Rizzo, M. Ruggieri, C. Zanetta, S. Brajkovic, H.M. Moulton, O. Müehlemann, N. Bresolin, G.P. Comi, S. Corti
Molecular, genetic and stem cell-mediated therapeutic strategies for spinal muscular atrophy (SMA)
2014-01-01 C. Zanetta, G. Riboldi, M. Nizzardo, C. Simone, I. Faravelli, N. Bresolin, G.P. Comi, S. Corti
Stem cell transplantation for amyotrophic lateral sclerosis: therapeutic potential and perspectives on clinical translation
2014-04-04 I. Faravelli, G. Riboldi, M. Nizzardo, C. Simone, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
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