Sfoglia per Autore
IGHMBP2 related pathological pathways in Spinal Muscular Atrophy with Respiratory Distress type 1 (SMARD1) in vitro models
2019 N. Galli, M. Taiana, E. Pagliari, S. Ghezzi, G. Comi, S. Corti, M. Nizzardo
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients
2019 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, G. Comi, S. Corti, M. Nizzardo
Optimization of AAV9 gene therapy for Spinal Muscular Atrophy with respiratory distress Type 1 using in vivo disease models
2020 E. Pagliari, P. Rinchetti, N. Galli, S. Ghezzi, M. Taiana, G. Comi, S. Corti, M. Nizzardo
Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
2020 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, D. Saccomanno, H.M. Moulton, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients
2020 E. Pagliari, M. Bersani, M. Rizzuti, A. Bordoni, D. Saccomanno, N. Bresolin, G. Comi, S. Corti, M. Nizzardo
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
2021 M. Bersani, M. Rizzuti, E. Pagliari, M. Garbellini, D. Saccomanno, H.M. Moulton, N. Bresolin, G.P. Comi, S. Corti, M. Nizzardo
Impairment of the neurotrophic signaling hub B-Raf contributes to motoneuron degeneration in spinal muscular atrophy
2021 N. Hensel, F. Cieri, P. Santonicola, I. Tapken, T. Schüning, M. Taiana, E. Pagliari, A. Joseph, S. Fischer, N. Heidrich, H. Brinkmann, S. Kubinski, A.K. Bergmann, M.F. Richter, K. Jung, S. Corti, E. Di Schiavi, P. Claus
Stathmins and Motor Neuron Diseases: Pathophysiology and Therapeutic Targets
2022 D. Gagliardi, E. Pagliari, M. Meneri, V. Melzi, F. Rizzo, G.P. Comi, S.P. Corti, M.M. Taiana, M. Nizzardo
OPTIMIZATION OF AAV9 GENE THERAPY FOR SPINAL MUSCULAR ATROPHY WITH RESPIRATORY DISTRESS TYPE 1 USING IN VIVO DISEASE MODELS
2023 E. Pagliari
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