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Mostrati risultati da 1 a 13 di 13
Titolo Data di pubblicazione Autori Tipo File Abstract
Peptide-conjugated Morpholino Oligomers for treatment of Spinal Muscular Atrophy 2016 A. RamirezM. RizzutiF. RizzoP. RinchettiM. BucchiaN. BresolinG. P. ComiS. CortiM. Nizzardo Conference Object -
Intracerebroventricular delivery in mice for motor neuron diseases 2017 Nizzardo, M.Rizzuti, M. Book Part (author) -
MicroRNA Metabolism and Dysregulation in Amyotrophic Lateral Sclerosis 2017 P. RinchettiM. RizzutiI. FaravelliS. Corti Article (author) -
Investigation of new morpholino oligomers to increase survival motor neuron protein levels in spinal muscular atrophy 2018 Ramirez, AgneseCRISAFULLI, SEBASTIANO GIUSEPPERizzuti, MafaldaBresolin, NereoComi, Giacomo P.Corti, StefaniaNizzardo, Monica Article (author) -
MicroRNA expression analysis identifies a subset of downregulated miRNAs in ALS motor neuron progenitors 2018 Rizzuti, MafaldaDioni, LauraBollati, ValentinaBresolin, NereoComi, Giacomo PietroNizzardo, MonicaCorti, Stefania + Article (author) -
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients 2019 Pagliari E.Bersani M.Rizzuti M.Bordoni A.Comi GP.Corti S.Nizzardo M. Conference Object -
miR-129-5p: A key factor and therapeutic target in amyotrophic lateral sclerosis 2020 Nizzardo, MonicaRizzuti, MafaldaCorti, Stefania + Article (author) -
Cell Penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model 2020 Pagliari E.Bersani M.Rizzuti M.Bordoni A.Bresolin N.Comi G. P.Corti S.Nizzardo M. + Conference Object -
CPPs-conjugated antisense nucleotides : a new therapeutic strategy for Spinal Muscular Atrophy symptomatic patients 2020 E. PagliariM. BersaniM. RizzutiA. BordoniN. BresolinGP. ComiS. CortiM. Nizzardo + Conference Object -
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model 2021 Bersani M.Rizzuti M.Pagliari E.Bresolin N.Comi G. P.Corti S.Nizzardo M. + Article (author) -
Insights into the identification of a molecular signature for amyotrophic lateral sclerosis exploiting integrated microRNA profiling of iPSC-derived motor neurons and exosomes 2022 Rizzuti M.Gagliardi D.Meneri M.Dioni L.Locatelli M.Biella F.Bollati V.Bresolin N.Comi G. P.Corti S. + Article (author) -
Genomic and transcriptomic advances in amyotrophic lateral sclerosis 2023 Rizzuti, MafaldaScarcella, SimoneCostamagna, GianlucaOttoboni, LindaVerde, FedericoRatti, AntoniaTicozzi, NicolaComi, Giacomo PietroCorti, StefaniaGagliardi, Delia + Article (author) -
Shaping the Neurovascular Unit Exploiting Human Brain Organoids 2024 Rizzuti, MafaldaBrambilla, LorenzoOttoboni, LindaMeneri, MegiRatti, AntoniaVerde, FedericoTicozzi, NicolaComi, Giacomo PietroCorti, StefaniaAbati, Elena + Article (author) -
Mostrati risultati da 1 a 13 di 13
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