Sfoglia per Autore
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Stem cell-mediated exon skipping of the dystrophin gene by the bystander effect
2015 M. Meregalli, A. Farini, C. Sitzia, C. Beley, P. Razini, L.M. Cassinelli, F. Colleoni, P. Frattini, N. Santo, E. Galbiati, D. Prosperi, A. Tavelli, M. Belicchi, L. Garcia, Y. Torrente
Autologous intramuscular transplantation of engineered satellite cells induces exosomemediated systemic expression of Fukutin-Related Protein and rescues disease phenotype in a murine model of Limb-Girdle Muscular Dystrophy Type 2I.
2017 P. Frattini, C. Villa, F. De Santis, M. Meregalli, M. Belicchi, S. Erratico, P. Bella, M.T. Raimondi, Q. Lu, Y. Torrente
AUTOLOGOUS INTRAMUSCULAR TRANSPLANTATION OF ENGINEERED SATELLITE CELLS INDUCES EXOSOME-MEDIATED SYSTEMIC EXPRESSION OF FUKUTIN-RELATED PROTEIN AND RESCUES DISEASE PHENOTYPE IN A MURINE MODEL OF LIMB-GIRDLE MUSCULAR DYSTROPHY TYPE 2I
2018 P. Frattini
Mostrati risultati da 1 a 3 di 3
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