Sfoglia per Autore
A model for motor neuron degeneration and treatment of Spinal Muscular Atrophy using human induced pluripotent stem cells
2011 S. Corti, F. Magri, M. Nizzardo, C. Simone, M. Falcone, S. Salani, C. Donadoni, M. Nardini, G. Riboldi, G. Menozzi, C. Bonaglia, F. Rizzo, N. Bresolin, G. Comi
Targeted gene correction of spinal muscular atrophy induced pluripotent stem cells and motoneurons as cell source for therapy
2012 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Menozzi, C. Bonaglia, F. Rizzo, F. Magri, N. Bresolin, G.P. Comi
Genetic correction of spinal muscular atrophy-induced pluripotent stem cells and motoneurons as a disease model and cell source for transplantation
2012 G. Riboldi, M. Nizzardo, M. Nardini, C. Simone, M. Falcone, D. Ronchi, C. Donadoni, S. Salani, F. Magri, F. Rizzo, M. Ranieri, A. Govoni, I. Faravelli, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
Research advances in gene therapy approaches for the treatment of amyotrophic lateral sclerosis
2012 M. Nizzardo, C. Simone, M. Falcone, G. Riboldi, F. Rizzo, F. Magri, N. Bresolin, G. P. Comi, S. Corti
Generation of skeletal muscle cells from embryonic and induced pluripotent stem cells as an in vitro model and for therapy of muscular dystrophies
2012 S. Salani, C. Donadoni, F. Rizzo, N. Bresolin, G.P. Comi, S. Corti
Direct reprogramming of human astrocytes into neural stem cells and neurons
2012 S. Corti, M. Nizzardo, C. Simone, M. Falcone, C. Donadoni, S. Salani, F. Rizzo, M. Nardini, G. Riboldi, F. Magri, C. Zanetta, I. Faravelli, N. Bresolin, G.P. Comi
Genetic correction of human induced pluripotent stem cells from patients with spinal muscular atrophy
2012 S. Corti, M. Nizzardo, C. Simone, M. Falcone, M. Nardini, D. Ronchi, C. Donadoni, S. Salani, G. Riboldi, F. Magri, G. Menozzi, C. Bonaglia, F. Rizzo, N. Bresolin, G.P. Comi
Development of a therapeutic approach for Spinal Muscular Atrophy with Respiratory Distress (SMARD1) using human induced pluripotent stem cell-derived neural stem cells and motor neurons
2013 S. C. Nizzardo M., F. Rizzo, M. Ruggieri, S. Salani, . Brajkovics, N. Bresolin, S. Corti
Mitochondrial fusion proteins and human diseases
2013 M. Ranieri, S. Brajkovic, G. Riboldi, D. Ronchi, F. Rizzo, N. Bresolin, S. Corti, G.P. Comi
Minimally invasive transplantation of iPSC-derived ALDHhiSSCloVLA4+ neural stem cells effectively improves the phenotype of an amyotrophic lateral sclerosis model
2014 M. Nizzardo, C. Simone, F. Rizzo, M. Ruggieri, S. Salani, G. Riboldi, I. Faravelli, C. Zanetta, N. Bresolin, G.P. Comi, S. Corti
Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy δ7 mouse model phenotype
2014 M. Nizzardo, C. Simone, S. Salani, M. Ruepp, F. Rizzo, M. Ruggieri, C. Zanetta, S. Brajkovic, H.M. Moulton, O. Müehlemann, N. Bresolin, G.P. Comi, S. Corti
Cellular therapy to target neuroinflammation in amyotrophic lateral sclerosis
2014 F. Rizzo, G. Riboldi, S. Salani, M. Nizzardo, C. Simone, S. Corti, E. Hedlund
IPSC-derived neural stem cells act via kinase inhibition to exert neuroprotective effects in spinal muscular atrophy with respiratory distress type 1
2014 C. Simone, M. Nizzardo, F. Rizzo, M. Ruggieri, G. Riboldi, S. Salani, M. Bucchia, N. Bresolin, G.P. Comi, S. Corti
Morpholino antisense oligomer against SOD1 for amyotrophic lateral sclerosis therapy
2015 C. Simone, M. Nizzardo, F. Rizzo, G. Ulzi, A. Ramirez, M. Bucchia, A. Bordoni, G. Comi, S. Corti
Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model
2015 M. Nizzardo, C. Simone, F. Rizzo, S. Salani, P. Rinchetti, R. Del Bo, S. Dametti, K. Foust, B. Kaspar, N. Bresolin, G. Comi, S. Corti
Spinal muscular atrophy phenotype is ameliorated in human motor neurons by SMN increase via different novel RNA therapeutic approaches
2015 M. Nizzardo, C. Simone, S. Dametti, S. Salani, G. Ulzi, S. Pagliarani, F. Rizzo, E. Frattini, F. Pagani, N. Bresolin, G. Comi, S. Corti
GENERAZIONE DI IPSC COME MODELLO IN VITRO E SVILUPPO DI UN POSSIBILE APPROCCIO TERAPEUTICO PER LA MALATTIA DI CHARCHOT-MARIE-TOOTH DI TIPO 2A(CMT2A)
2015 F. Rizzo
Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model
2015 M. Nizzardo, C. Simone, F. Rizzo, S. Salani, S. Dametti, P. Rinchetti, R. Del Bo, K. Foust, B.K. Kaspar, N. Bresolin, G.P. Comi, S. Corti
MFN2-related neuropathies: clinical features, molecular pathogenesis and therapeutic perspectives
2015 G. Stuppia, F. Rizzo, G. Riboldi, R. Del Bo, M. Nizzardo, C. Simone, G.P. Comi, N. Bresolin, S. Corti
Morpholino-mediated SOD1 reduction ameliorates an amyotrophic lateral sclerosis disease phenotype
2016 M. Nizzardo, C. Simone, F. Rizzo, G. Ulzi, A. Ramirez, M. Rizzuti, A. Bordoni, M. Bucchia, S. Gatti, N. Bresolin, G.P. Comi, S. Corti
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