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Mostrati risultati da 1 a 20 di 31
Titolo Data di pubblicazione Autori Tipo File Abstract
A model for motor neuron degeneration and treatment of Spinal Muscular Atrophy using human induced pluripotent stem cells 2011 S. CortiF. MagriM. NizzardoC. SimoneM. FalconeS. SalaniC. DonadoniM. NardiniRIBOLDI, GIOVANNAF. RizzoN. BresolinG. Comi + Article (author) -
Targeted gene correction of spinal muscular atrophy induced pluripotent stem cells and motoneurons as cell source for therapy 2012 S. CortiM. NizzardoC. SimoneM. FalconeM. NardiniD. RonchiS. SalaniF. RizzoF. MagriN. BresolinG.P. Comi + Article (author) -
Genetic correction of spinal muscular atrophy-induced pluripotent stem cells and motoneurons as a disease model and cell source for transplantation 2012 G. RiboldiM. NizzardoM. NardiniC. SimoneM. FalconeD. RonchiS. SalaniF. MagriF. RizzoA. GovoniI. FaravelliN. BresolinG.P. ComiS. Corti + Article (author) -
Research advances in gene therapy approaches for the treatment of amyotrophic lateral sclerosis 2012 M. NizzardoC. SimoneM. FalconeG. RiboldiF. RizzoF. MagriN. BresolinG. P. ComiS. Corti Article (author) -
Generation of skeletal muscle cells from embryonic and induced pluripotent stem cells as an in vitro model and for therapy of muscular dystrophies 2012 S. SalaniF. RizzoN. BresolinG.P. ComiS. Corti + Article (author) -
Direct reprogramming of human astrocytes into neural stem cells and neurons 2012 S. CortiM. NizzardoC. SimoneM. FalconeS. SalaniF. RizzoG. RiboldiF. MagriI. FaravelliN. BresolinG.P. Comi + Article (author) -
Genetic correction of human induced pluripotent stem cells from patients with spinal muscular atrophy 2012 S. CortiM. NizzardoC. SimoneD. RonchiF. MagriF. RizzoN. BresolinG. P. Comi + Article (author) -
Development of a therapeutic approach for Spinal Muscular Atrophy with Respiratory Distress (SMARD1) using human induced pluripotent stem cell-derived neural stem cells and motor neurons 2013 F. RizzoM. RuggieriS. SalaniN. BresolinS. Corti + Conference Object -
Mitochondrial fusion proteins and human diseases 2013 M. RanieriG. RiboldiD. RonchiF. RizzoN. BresolinS. CortiG.P. Comi + Article (author) -
Minimally invasive transplantation of iPSC-derived ALDHhiSSCloVLA4+ neural stem cells effectively improves the phenotype of an amyotrophic lateral sclerosis model 2014 M. NizzardoC. SimoneF. RizzoS. SalaniG. RiboldiI. FaravelliN. BresolinG.P. ComiS. Corti + Article (author) -
Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy δ7 mouse model phenotype 2014 M. NizzardoC. SimoneS. SalaniF. RizzoN. BresolinG.P. ComiS. Corti + Article (author) -
Cellular therapy to target neuroinflammation in amyotrophic lateral sclerosis 2014 F. RizzoG. RiboldiS. SalaniM. NizzardoC. SimoneS. Corti + Article (author) -
IPSC-derived neural stem cells act via kinase inhibition to exert neuroprotective effects in spinal muscular atrophy with respiratory distress type 1 2014 C. SimoneM. NizzardoF. RizzoG. RiboldiS. SalaniM. BucchiaN. BresolinG.P. ComiS. Corti + Article (author) -
Morpholino antisense oligomer against SOD1 for amyotrophic lateral sclerosis therapy 2015 F. RizzoG. UlziA. RamirezM. BucchiaA. BordoniG. ComiS. Corti + Conference Object -
Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model 2015 M. NizzardoC. SimoneF. RizzoS. SalaniP. RinchettiR. Del BoS. DamettiN. BresolinG. ComiS. Corti + Conference Object -
Spinal muscular atrophy phenotype is ameliorated in human motor neurons by SMN increase via different novel RNA therapeutic approaches 2015 M. NizzardoC. SimoneS. DamettiS. SalaniG. UlziS. PagliaraniF. RizzoE. FrattiniN. BresolinG. ComiS. Corti + Article (author) -
GENERAZIONE DI IPSC COME MODELLO IN VITRO E SVILUPPO DI UN POSSIBILE APPROCCIO TERAPEUTICO PER LA MALATTIA DI CHARCHOT-MARIE-TOOTH DI TIPO 2A(CMT2A) 2015 F. Rizzo Doctoral Thesis -
Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model 2015 M. NizzardoC. SimoneF. RizzoS. SalaniS. DamettiP. RinchettiR. Del BoN. BresolinG.P. ComiS. Corti + Article (author) -
MFN2-related neuropathies: clinical features, molecular pathogenesis and therapeutic perspectives 2015 F. RizzoG. RiboldiR. Del BoM. NizzardoC. SimoneG.P. ComiN. BresolinS. Corti + Article (author) -
Morpholino-mediated SOD1 reduction ameliorates an amyotrophic lateral sclerosis disease phenotype 2016 M. NizzardoC. SimoneF. RizzoG. UlziA. RamirezA. BordoniM. BucchiaN. BresolinG.P. ComiS. Corti + Article (author) -
Mostrati risultati da 1 a 20 di 31
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